J&J jumps on the MFN pricing train

J&J jumps on the MFN pricing train

[ad_1] Johnson & Johnson is the latest pharma group to agree a Most-Favoured Nation (MFN) drug pricing agreement with the Trump administration to avert the threat of tariffs. In a statement, the company – thought to be the 15th to sign up to such a deal – said it will deliver improved access to medicines…

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CIRM awards .4 million to advance stem cell-based gene therapy for Friedreich’s ataxia

CIRM awards $7.4 million to advance stem cell-based gene therapy for Friedreich’s ataxia

[ad_1] The California Institute for Regenerative Medicine (CIRM) has awarded $7.4 million to support a University of California San Diego team developing a first-of-its-kind stem cell-based gene therapy for Friedreich’s ataxia, a rare inherited neurodegenerative disease that causes progressive loss of coordination, muscle strength, heart function and overall mobility. The new funding will help the…

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Recent advances in CAR-NK cell therapy could revolutionze cancer treatment

Recent advances in CAR-NK cell therapy could revolutionze cancer treatment

[ad_1] Cell-based immunotherapies have transformed cancer treatment, yet their widespread use remains constrained by safety risks, manufacturing complexity, and limited effectiveness against solid tumors. CAR-T cell therapy, while highly effective in certain blood cancers, is frequently associated with cytokine release syndrome, neurotoxicity, and prolonged production timelines. These challenges highlight the need for alternative immune cell…

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Experimental gene therapy restores immune system function in children with genetic immune disorder

Experimental gene therapy restores immune system function in children with genetic immune disorder

[ad_1] An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has restored and maintained immune system function in 59 of 62 children born with ADA-SCID, a rare and deadly genetic immune disorder. Severe combined immunodeficiency due to adenosine deaminase deficiency, or ADA-SCID, is caused by mutations in the…

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